Duchenne Muscular Dystrophy - Pipeline Review, H2 2019

Publisher Name :
Date: 25-Nov-2019
No. of pages: 330
Inquire Before Buying

Duchenne Muscular Dystrophy - Pipeline Review, H2 2019

Summary

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Duchenne Muscular Dystrophy - Pipeline Review, H2 2019, provides an overview of the Duchenne Muscular Dystrophy (Genetic Disorders) pipeline landscape.

Duchenne muscular dystrophy (DMD) is a genetic disorder that causes muscles to gradually weaken over time. Signs and symptoms of DMD include fatigue, learning difficulties, intellectual disability, muscle weakness and progressive difficulty walking. Risk factors include gender and family history. Treatment includes steroid medication, respiratory therapy and surgery.

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Duchenne Muscular Dystrophy - Pipeline Review, H2 2019, provides comprehensive information on the therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide also reviews of key players involved in therapeutic development for Duchenne Muscular Dystrophy and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Filing rejected/Withdrawn, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 2, 3, 4, 13, 8, 1, 51, 24 and 1 respectively. Similarly, the Universities portfolio in Phase III, Phase II, Phase I, Preclinical and Discovery stages comprises 2, 1, 1, 10 and 2 molecules, respectively.

Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct's proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

- The pipeline guide provides a snapshot of the global therapeutic landscape of Duchenne Muscular Dystrophy (Genetic Disorders).

- The pipeline guide reviews pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.

- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.

- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.

- The pipeline guide reviews key companies involved in Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics and enlists all their major and minor projects.

- The pipeline guide evaluates Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.

- The pipeline guide encapsulates all the dormant and discontinued pipeline projects.

- The pipeline guide reviews latest news related to pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders)

Reasons to buy

- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.

- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.

- Find and recognize significant and varied types of therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders).

- Classify potential new clients or partners in the target demographic.

- Develop tactical initiatives by understanding the focus areas of leading companies.

- Plan mergers and acquisitions meritoriously by identifying key players and it's most promising pipeline therapeutics.

- Formulate corrective measures for pipeline projects by understanding Duchenne Muscular Dystrophy (Genetic Disorders) pipeline depth and focus of Indication therapeutics.

- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.

- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.

Duchenne Muscular Dystrophy - Pipeline Review, H2 2019

Table of Contents
Introduction
Duchenne Muscular Dystrophy - Overview
Duchenne Muscular Dystrophy - Therapeutics Development
Duchenne Muscular Dystrophy - Therapeutics Assessment
Duchenne Muscular Dystrophy - Companies Involved in Therapeutics Development
Duchenne Muscular Dystrophy - Drug Profiles
Duchenne Muscular Dystrophy - Dormant Projects
Duchenne Muscular Dystrophy - Discontinued Products
Duchenne Muscular Dystrophy - Product Development Milestones
Appendix

List of Tables
Table 1: Number of Products under Development for Duchenne Muscular Dystrophy, H2 2019
Table 2: Number of Products under Development by Companies, H2 2019
Table 3: Number of Products under Development by Companies, H2 2019 (Contd..1), H2 2019
Table 4: Number of Products under Development by Companies, H2 2019 (Contd..2), H2 2019
Table 5: Number of Products under Development by Companies, H2 2019 (Contd..3), H2 2019
Table 6: Number of Products under Development by Universities/Institutes, H2 2019
Table 7: Products under Development by Companies, H2 2019
Table 8: Products under Development by Companies, H2 2019 (Contd..1), H2 2019
Table 9: Products under Development by Companies, H2 2019 (Contd..2), H2 2019
Table 10: Products under Development by Companies, H2 2019 (Contd..3), H2 2019
Table 11: Products under Development by Companies, H2 2019 (Contd..4), H2 2019
Table 12: Products under Development by Companies, H2 2019 (Contd..5), H2 2019
Table 13: Products under Development by Companies, H2 2019 (Contd..6), H2 2019
Table 14: Products under Development by Universities/Institutes, H2 2019
Table 15: Number of Products by Stage and Target, H2 2019
Table 16: Number of Products by Stage and Target, H2 2019 (Contd..1), H2 2019
Table 17: Number of Products by Stage and Mechanism of Action, H2 2019
Table 18: Number of Products by Stage and Mechanism of Action, H2 2019 (Contd..1), H2 2019
Table 19: Number of Products by Stage and Route of Administration, H2 2019
Table 20: Number of Products by Stage and Molecule Type, H2 2019
Table 21: Duchenne Muscular Dystrophy - Pipeline by 4D Molecular Therapeutics Inc, H2 2019
Table 22: Duchenne Muscular Dystrophy - Pipeline by Advanced Medical Projects, H2 2019
Table 23: Duchenne Muscular Dystrophy - Pipeline by Akashi Therapeutics Inc, H2 2019
Table 24: Duchenne Muscular Dystrophy - Pipeline by Alpha Anomeric, H2 2019
Table 25: Duchenne Muscular Dystrophy - Pipeline by Anagenesis Biotechnologies SAS, H2 2019
Table 26: Duchenne Muscular Dystrophy - Pipeline by Antisense Therapeutics Ltd, H2 2019
Table 27: Duchenne Muscular Dystrophy - Pipeline by Armgo Pharma Inc, H2 2019
Table 28: Duchenne Muscular Dystrophy - Pipeline by Audentes Therapeutics Inc, H2 2019
Table 29: Duchenne Muscular Dystrophy - Pipeline by AUM LifeTech Inc, H2 2019
Table 30: Duchenne Muscular Dystrophy - Pipeline by Avidity Biosciences LLC, H2 2019
Table 31: Duchenne Muscular Dystrophy - Pipeline by Axolo Pharma Inc, H2 2019
Table 32: Duchenne Muscular Dystrophy - Pipeline by Beech Tree Labs Inc, H2 2019
Table 33: Duchenne Muscular Dystrophy - Pipeline by Biogen Inc, H2 2019
Table 34: Duchenne Muscular Dystrophy - Pipeline by Bioleaders Corp, H2 2019
Table 35: Duchenne Muscular Dystrophy - Pipeline by Biophytis SA, H2 2019
Table 36: Duchenne Muscular Dystrophy - Pipeline by Capricor Therapeutics Inc, H2 2019
Table 37: Duchenne Muscular Dystrophy - Pipeline by Cardero Therapeutics Inc, H2 2019
Table 38: Duchenne Muscular Dystrophy - Pipeline by Catabasis Pharmaceuticals Inc, H2 2019
Table 39: Duchenne Muscular Dystrophy - Pipeline by Consortium.AI, H2 2019
Table 40: Duchenne Muscular Dystrophy - Pipeline by Constant Therapeutics LLC, H2 2019
Table 41: Duchenne Muscular Dystrophy - Pipeline by CRISPR Therapeutics AG, H2 2019
Table 42: Duchenne Muscular Dystrophy - Pipeline by Cumberland Pharmaceuticals Inc, H2 2019
Table 43: Duchenne Muscular Dystrophy - Pipeline by Daiichi Sankyo Co Ltd, H2 2019
Table 44: Duchenne Muscular Dystrophy - Pipeline by DepYmed Inc, H2 2019
Table 45: Duchenne Muscular Dystrophy - Pipeline by DMD Therapeutics Inc, H2 2019
Table 46: Duchenne Muscular Dystrophy - Pipeline by Dyne Therapeutics Inc, H2 2019
Table 47: Duchenne Muscular Dystrophy - Pipeline by Dystrogen Therapeutics SA, H2 2019
Table 48: Duchenne Muscular Dystrophy - Pipeline by Edgewise Therapeutics, H2 2019
Table 49: Duchenne Muscular Dystrophy - Pipeline by Editas Medicine Inc, H2 2019
Table 50: Duchenne Muscular Dystrophy - Pipeline by Eloxx Pharmaceuticals Inc, H2 2019
Table 51: Duchenne Muscular Dystrophy - Pipeline by Evox Therapeutics Ltd, H2 2019
Table 52: Duchenne Muscular Dystrophy - Pipeline by FibroGen Inc, H2 2019
Table 53: Duchenne Muscular Dystrophy - Pipeline by Fulcrum Therapeutics Inc, H2 2019
Table 54: Duchenne Muscular Dystrophy - Pipeline by Galapagos NV, H2 2019
Table 55: Duchenne Muscular Dystrophy - Pipeline by Hibernaid Inc, H2 2019
Table 56: Duchenne Muscular Dystrophy - Pipeline by InnoBioscience LLC, H2 2019
Table 57: Duchenne Muscular Dystrophy - Pipeline by Italfarmaco SpA, H2 2019
Table 58: Duchenne Muscular Dystrophy - Pipeline by Keros Therapeutics Inc, H2 2019
Table 59: Duchenne Muscular Dystrophy - Pipeline by LambdaGen Therapeutics, H2 2019
Table 60: Duchenne Muscular Dystrophy - Pipeline by Milo Biotechnology LLC, H2 2019

List of Figures
Figure 1: Number of Products under Development for Duchenne Muscular Dystrophy, H2 2019
Figure 2: Number of Products under Development by Companies, H2 2019
Figure 3: Number of Products under Development by Universities/Institutes, H2 2019
Figure 4: Number of Products by Targets, H2 2019
Figure 5: Number of Products by Stage and Targets, H2 2019
Figure 6: Number of Products by Mechanism of Actions, H2 2019
Figure 7: Number of Products by Stage and Mechanism of Actions, H2 2019
Figure 8: Number of Products by Routes of Administration, H2 2019
Figure 9: Number of Products by Stage and Routes of Administration, H2 2019
Figure 10: Number of Products by Top 10 Molecule Types, H2 2019
Figure 11: Number of Products by Stage and Top 10 Molecule Types, H2 2019
  • Global Genome Editing Industry Research Report, In-depth Analysis of Current Status and Outlook of Key Countries 2023-2028
    Published: 16-Nov-2023        Price: US 3380 Onwards        Pages: 111
    Market Overview of Global Genome Editing market: According to our latest research, the global Genome Editing market looks promising in the next 5 years. As of 2022, the global Genome Editing market was estimated at USD 7377.87 million, and it's anticipated to reach USD 25474.29 million in 2028, with a CAGR of 22.94% during the forecast years. Genome editing is a type of genetic engineering in which DNA is inserted, deleted, modified or replaced in the genome of a living organ......
  • Global Genome Editing Market Insights, Forecast to 2029
    Published: 14-Aug-2023        Price: US 4900 Onwards        Pages: 86
    Genome editing, or genome engineering is a type of genetic engineering in which DNA is inserted, deleted, modified or replaced in the genome of a living organism. In 2018, the common methods for such editing use engineered nucleases, or "molecular scissors". These nucleases create site-specific double-strand breaks (DSBs) at desired locations in the genome. The induced double-strand breaks are repaired through nonhomologous end-joining (NHEJ) or homologous recombination (HR), resulting in target......
  • Animal Genetics Market by Product (Live Animal (Poultry, Porcine, Bovine, Canine) Genetic Material (Semen (Bovine, Porcine, Equine), Embryo (Bovine, Equine)) Genetic Testing Service (Disease, Genetic Traits - Bovine, DNA Typing)) - Global Forecast to 2028
    Published: 10-Aug-2023        Price: US 4950 Onwards        Pages: 320
    Rising demand for livestock animals due to the growing population, increasing per capita income, and rapid urbanization will drive the market growth. The global animal genetics market is projected to reach USD 9.5 billion by 2028 from USD 6.6 billion in 2023, at a CAGR of 7.4% during the forecast period. The increasing consumption of animal products, adoption of advanced genetic testing methods, animal welfare activities, and demand for companion animals are fueling the growth of this......
  • Epigenetic Therapeutics: Global Markets
    Published: 01-Jun-2023        Price: US 5500 Onwards        Pages: 155
    Report Scope: This report is a comprehensive study of the global market for epigenetic therapeutics. It describes the epigenetic therapeutics market, which is segmented by product type and region. Based on product type, the market is segmented into PRAP inhibitors, Kinase inhibitors, IDH inhibitors, HDAC inhibitors, DNMT inhibitors and KMT inhibitors. The market is segmented by region into North America, Latin America, Europe, Asia-Pacific, and the Rest of the World (RoW). ......
  • Genome Editing Market Growth Analysis Report - Latest Trends, Driving Factors and Key Players Research to 2030
    Published: 05-May-2023        Price: US 4150 Onwards        Pages: 146
    The study predicts the short term and long term trends that can shape up the future of the Genome Editing market including the COVID-19 pandemic implications for Genome Editings industry. The report presents market size forecasts across types, applications, end users and countries across regions. Strategic imperatives for development managers, decision makers and industry professionals including market trends, drivers, challenges, five forces analysis, insights on markets and companies. ......
  • Global Genome Editing Market Insights: Impact of COVID-19 and Future Expectations to 2028
    Published: 16-Mar-2023        Price: US 3260 Onwards        Pages: 95
    Genome editing is a type of genetic engineering in which DNA is inserted, deleted, modified or replaced in the genome of a living organism. Unlike early genetic engineering techniques that randomly inserts genetic material into a host genome, genome editing targets the insertions to site specific locations. The Genome Editing market revenue was 7377.87 Million USD in 2022, and will reach 25474.29 Million USD in 2028, with a CAGR of 22.94% during 2022-2028. This report elabo......
  • Global Genome Editing/Genome Engineering Market Status and Outlook 2023-2028
    Published: 01-Mar-2023        Price: US 3160 Onwards        Pages: 108
    Genome editing, or genome engineering, or gene editing, is a type of genetic engineering in which DNA is inserted, deleted, modified or replaced in the genome of a living organism. Our market research experts provide qualitative and quantitative analysis of the market based on involving economic and non-economic factors in the same report with market value (million USD) data for each segment and sub-segment. This way, clients can achieve all their goals while taking advantage of emerging ......
  • Global Genome Engineering Market Status and Outlook 2023-2028
    Published: 23-Feb-2023        Price: US 3160 Onwards        Pages: 107
    Genome editing, or genome engineering, or gene editing, is a type of genetic engineering in which DNA is inserted, deleted, modified or replaced in the genome of a living organism. Unlike early genetic engineering techniques that randomly inserts genetic material into a host genome, genome editing targets the insertions to site specific locations. Our market research experts provide qualitative and quantitative analysis of the market based on involving economic and non-economic factors in......
  • Global Genome Editing Market Research Report 2023
    Published: 07-Feb-2023        Price: US 2900 Onwards        Pages: 85
    Genome editing, or genome engineering is a type of genetic engineering in which DNA is inserted, deleted, modified or replaced in the genome of a living organism. In 2018, the common methods for such editing use engineered nucleases, or "molecular scissors". These nucleases create site-specific double-strand breaks (DSBs) at desired locations in the genome. The induced double-strand breaks are repaired through nonhomologous end-joining (NHEJ) or homologous recombination (HR), resulting in target......
  • SERVICES
    Value for Money
    We believe in "optimum utilization of available budget and resources". While servicing our clients' (your) market research requirements, we keep the same approach in focus to help you get the best value for your $$s.
    Ever Growing Inventory
    Ranging from the smallest feasible / required data (datasheets, data facts, SWOT analysis, company profiles, etc) to full research reports that help you make decisions, our inventory is updated almost on a daily basis with the latest industry reports from domain experts that track more than 5000 niche sectors.
    One Stop Solution
    Need a custom research report on medical devices market? Require all available business intelligence on 3D printing industry? Exploring F&B sector of a particular country/region? RnRMarketResearch.com is your one-stop-solution to all market intelligence needs. We not only offer custom research and consulting services, we also "bundle" reports to meet your needs and help you fetch the data analysis you require for your business.
    Dedicated Client Engagement
    Not limited to only "finding" relevant reports for you, our client engagement team dedicates its efforts to understand your "business need" and accordingly maps available research data to help you move forward. Call "your" client engagement executive any time of your day and get your questions answered in order to make the correct business decision.
    Saving Time and Efforts
    Simply share your research requirement details with us and let us do all the hard work to find required intelligence for you. When you add up our "one stop solution" and "dedicated client engagement" services mentioned above, you obviously know the time and effort saving you do by working with us.
    Payment Flexibility
    Working with Fortune 500 organizations, we understand the importance of being flexible for payments. Share your payment terms with us and we will surely match up to them to ensure you get access to required business intelligence data without having to wait for the payment to be done.
    Post-Purchase Research Support
    Have questions after reading a report / datasheet bought through us? Not sure about the methodology used for data available in the research? Talk to us / Share your questions with us and if required, we will connect you with the analyst(s)/author(s) of the report(s) and ensure you get satisfactory answers for the same. Need more data / analysis / report(s) on the topic of your research/project? The RnRMarketResearch.com team is here for you 24X7 to support you with your post-purchase requirements. Subscription Offers & Packages (Get in touch with us for more details - [email protected] / +1 888 391 5441 )
    • Ad Hoc
    • Pay - as - you - go / Bucket Subscriptions
    • Fixed Cost for #of reports
    • Customize / Personalize as per your needs