Global Orphan Drugs Market: Industry Analysis & Outlook (2018-2022)

Publisher Name :
Date: 23-Jul-2018
No. of pages: 79
Inquire Before Buying

Orphan diseases are typically life-threatening or chronically debilitating for which no or inadequate alternative treatments are available. An orphan disease refers to any rare disease which affects a smaller share of population. Most of the rare diseases are genetic and therefore chronic. Presently, there are around 7000 rare diseases affecting approximately 5-6% of the global population. Half of the population of orphan disease patients is children as most of the genetic orphan diseases occur at birth or childhood.

Generally, orphan diseases are considered to be severe, progressive, degenerative, life-threatening or chronically debilitating diseases which can be caused genetically, infectiously or toxically. Despite knowing the causes of orphan diseases, most of these diseases are still non-curable or lack satisfactory treatments. Majority of the genetic orphan diseases are caused by defects in a single gene due to multiple mutations.

Orphan drug market is likely to witness a growth in future with increasing development and approvals of ultra-rare drugs and rising developments in drugs for rare blood disease. The US and Europe are the major contributors to the global orphan drugs market supported by increased numbers of orphan drug designations. Asia is likely to experience further growth with increasing orphan designations in Japan and improving healthcare facilities.

The global orphan drugs market is expected to grow in future due to prolonged orphan drug market exclusivity, increasing sales of prescription drugs, attractive orphan drug policies, rising healthcare expenditure, improving economies and increasing prevalence of chronic diseases. Key trends & development of this market include rise in orphan drug approvals, accelerating pipeline sales of orphan drugs, development of drug therapies and rising scope in gene therapy. However, there are some factors which can hinder growth of the market including high costs of drugs, increased competition from generic industry, insufficient disease information & research participants and deficiency of diagnostic systems and trained professionals.

The report “Global Orphan Drugs Market: Industry Analysis & Outlook (2018-2022)” by Koncept Analytics provides an extensive research and detailed analysis of the present market along with future outlook. The report discusses the major growth drivers and challenges of the market, covering the US, Europe and Asia along with the global market. The report profiles key players of the market including Roche holding AF, Novartis International AG, Bristol-Myers Squibb and Celgene Corporation.

Global Orphan Drugs Market: Industry Analysis & Outlook (2018-2022)

Table of Contents

1. Overview
1.1 Orphan Disease
1.2 Orphan Drugs

2. Global Orphan Drugs Market
2.1 Global Orphan Drugs Market by Value
2.2 Global Orphan Drugs Market Forecast by Value
2.3 Global Orphan Drugs Market by Product
2.3.1 Global Revlimid Drug Revenue Forecast
2.3.2 Global Rituxan Drug Revenue Forecast
2.3.3 Global Opvido Drug Revenue Forecast
2.4 Global Orphan Drugs Market by Therapy
2.4.1 Global Oncology Therapy Market Forecast by Value
2.4.2 Global Blood Therapy Market Forecast by Value
2.4.3 Global Central Nervous System Therapy Market Forecast by Value

3. Regional Market Analysis
3.1 The Americas
3.1.1 The US Orphan Drugs Spending Forecast
3.1.2 The US Orphan Drug by Designation Volume
3.1.3 The US Orphan Drug Average & Median Cost per Patient
3.1.4 The US Orphan Drug Average & Median Cost per Patient Forecast
3.1.5 Canada Orphan Drugs Spending
3.1.6 Canada Orphan Drugs Spending Forecast
3.2 Europe
3.2.1 Europe Orphan Drugs Market Forecast by Value
3.2.2 Europe Orphan Drugs Market by Product
3.2.3 Europe Orphan Drug by Designation Volume
3.3 Asia
3.3.1 Japan Orphan Drug by Designation Volume
3.3.2 India Orphan Drugs Market Forecast by Value

4. Market Dynamics
4.1 Growth Drivers
4.1.1 Prolonged Orphan Drug Market Exclusivity
4.1.2 Increasing Sales of Prescription Drugs
4.1.3 Attractive Orphan Drug Policies
4.1.4 Rising Healthcare Expenditure
4.1.5 Improving Economic Condition
4.1.6 Increasing Prevalence of Chronic Diseases
4.2 Key Trends & Development
4.2.1 Rise in Orphan Drug Approvals
4.2.2 Accelerating Pipeline Sales of Orphan Drugs
4.2.3 Development of Drug Therapies
4.2.4 Increasing Scope of Gene Therapy
4.3 Challenges
4.3.1 High Costs
4.3.2 Lack of Diagnostic Systems and Trained Professionals
4.3.3 Insufficient Disease Information and Research Participants
4.3.4 Rising Competition from Generic Industry

5. Competitive Landscape
5.1 Global Market
5.1.1 Revenue and Market Cap Comparison
5.1.2 Global Orphan Drugs Market Share by Company
5.1.3 Global Oncology Orphan Drugs Market Share by Company
5.2 The US
5.2.1 The US Top 10 Orphan Drugs Sales by Company
5.3 Europe
5.3.1 Europe Orphan Drugs Market Share by Company

6. Company Profiles
6.1 Novartis International AG
6.1.1 Business Overview
6.1.2 Financial Overview
6.1.3 Business Strategies
6.2 Roche Holding AG
6.2.1 Business Overview
6.2.2 Financial Overview
6.2.3 Business Strategies
6.3 Bristol-Myers Squibb
6.3.1 Business Overview
6.3.2 Financial Overview
6.3.3 Business Strategies
6.4 Celgene Corporation
6.4.1 Business Overview
6.4.2 Financial Overview
6.4.3 Business Strategies

List of Tables

Orphan Disease Prevalence in Different Nations
Orphan Drug Market Exclusivity
Orphan Drug Policies
Prices and Prevalence of Some Orphan Drugs in the US (2017)
Key Players - Revenue & Market Cap Comparison (2017)
The US Top 10 Orphan Drugs Sales by Company (2017)
Novartis Agreements (2018)
Novartis Major Product Approvals (2018)
Roche Agreements (2017/2018)
Roche Product Approvals (2018)
Bristol-Myers Squibb Agreements (2018)
Celgene R&D Expenditure (2015-2017)

List of Charts

Types of Orphan Drugs
Orphan Drug Development
Global Orphan Drugs Market by Value (2013-2017)
Global Orphan Drugs Market Forecast by Value (2018-2022)
Global Orphan Drugs Market by Product (2017)
Global Revlimid Drug Revenue Forecast (2017-2022)
Global Rituxan Drug Revenue Forecast (2017-2022)
Global Opvido Drug Revenue Forecast (2017-2022)
Global Orphan Drugs Market by Therapy (2017)
Global Oncology Therapy Market Forecast by Value (2017-2022)
Global Blood Therapy Market Forecast by Value (2017-2022)
Global Central Nervous System Therapy Market Forecast by Value (2017-2022)
The US Orphan Drugs Spending Forecast (2017-2022)
The US Orphan Drug by Designation Volume (2013-2017)
The US Orphan Drug Average & Median Cost per Patient (2013-2017)
The US Orphan Drug Average & Median Cost per Patient Forecast (2018-2022)
Canada Orphan Drugs Spending (2013-2017)
Canada Orphan Drugs Spending Forecast (2018-2022)
Europe Orphan Drugs Market Forecast by Value (2017-2022)
Europe Orphan Drugs Market by Product (2017)
Europe Orphan Drug by Designation Volume (2013-2017)
Japan Orphan Drug by Designation Volume (2013-2017)
India Orphan Drugs Market Forecast by Value (2017-2022)
Global Prescription Drugs Sales (2013-2022)
Global Healthcare Expenditure (2013-2017)
Global GDP Per Capita (2013-2017)
Global Cancer Prevalence (2012-2030E)
The US FDA Orphan Drug Approvals (2010-2017)
The US Orphan Novel Drug Approvals (2010-2017)
Global Worldwide Orphan Drug Pipeline Sales (2018-2024)
Projection of Top 10 Orphan Drugs in Development (phase III/filed) by NPV* (2018)
Global Orphan Drugs Market Share by Company (2017/2024)
Global Oncology Orphan Drugs Market Share by Company (2017/2024)
Europe Orphan Drugs Market Share by Company (2017)
Novartis Sales by Segment (2017)
Novartis Net Sales and Net Income (2013-2017)
Roche Sales by Segments (2017)
Roche Sales and Net Income (2013-2017)
Bristol-Myers Squibb Revenue by Region (2017)
Bristol-Myers Squibb Total Revenue and Net Earnings (2013-2017)
Bristol-Myers Squibb R&D Expenditure (2015-2017)
Celgene Revenue by Region (2017)
Celgene Total Revenue and Net Income (2013-2017)

  • Global Antioxidant Vitamins Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 100
    The global Antioxidant Vitamins market was valued at US$ million in 2023 and is anticipated to reach US$ million by 2030, witnessing a CAGR of % during The forecast period 2024-2030. North American market for Antioxidant Vitamins is estimated to increase from $ million in 2023 to reach $ million by 2030, at a CAGR of % during The forecast period of 2024 through 2030. Asia-Pacific market for Antioxidant Vitamins is estimated to increase from $ million in 2023 to reach $ millio......
  • Global Clavulanate Potassium Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 86
    The global Clavulanate Potassium market was valued at US$ 446.6 million in 2023 and is anticipated to reach US$ 637.2 million by 2030, witnessing a CAGR of 5.2% during The forecast period 2024-2030. North American market for Clavulanate Potassium is estimated to increase from $ million in 2023 to reach $ million by 2030, at a CAGR of % during The forecast period of 2024 through 2030. Asia-Pacific market for Clavulanate Potassium is estimated to increase from $ million in 2023......
  • Global Amoxicillin Sodium Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 84
    The global Amoxicillin Sodium market was valued at US$ 460.9 million in 2023 and is anticipated to reach US$ 735.1 million by 2030, witnessing a CAGR of 7.0% during The forecast period 2024-2030. North American market for Amoxicillin Sodium is estimated to increase from $ million in 2023 to reach $ million by 2030, at a CAGR of % during The forecast period of 2024 through 2030. Asia-Pacific market for Amoxicillin Sodium is estimated to increase from $ million in 2023 to reach......
  • Global Melatonin Supplements Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 106
    The global Melatonin Supplements market was valued at US$ million in 2023 and is anticipated to reach US$ million by 2030, witnessing a CAGR of % during The forecast period 2024-2030. North American market for Melatonin Supplements is estimated to increase from $ million in 2023 to reach $ million by 2030, at a CAGR of % during The forecast period of 2024 through 2030. Asia-Pacific market for Melatonin Supplements is estimated to increase from $ million in 2023 to reach $ mil......
  • Global Sleeping Pills (Prescription Drugs) Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 93
    The global Sleeping Pills (Prescription Drugs) market was valued at US$ 1022.3 million in 2023 and is anticipated to reach US$ 1437.8 million by 2030, witnessing a CAGR of 4.9% during The forecast period 2024-2030. The global pharmaceutical market is 1475 billion USD in 2022, growing at a CAGR of 5% during The next six years. The pharmaceutical market includes chemical drugs and biological drugs. For biologics is expected to 381 billion USD in 2022. In comparison, The chemical......
  • Global Sleeping Pills Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 94
    The global Sleeping Pills market was valued at US$ 2042.3 million in 2023 and is anticipated to reach US$ 2979.5 million by 2030, witnessing a CAGR of 3.8% during The forecast period 2024-2030. The global pharmaceutical market is 1475 billion USD in 2022, growing at a CAGR of 5% during The next six years. The pharmaceutical market includes chemical drugs and biological drugs. For biologics is expected to 381 billion USD in 2022. In comparison, The chemical drug market is estim......
  • Global Zinc Oral Drops Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 85
    The global Zinc Oral Drops market was valued at US$ million in 2023 and is anticipated to reach US$ million by 2030, witnessing a CAGR of % during The forecast period 2024-2030. North American market for Zinc Oral Drops is estimated to increase from $ million in 2023 to reach $ million by 2030, at a CAGR of % during The forecast period of 2024 through 2030. Asia-Pacific market for Zinc Oral Drops is estimated to increase from $ million in 2023 to reach $ million by 2030, at a......
  • Global Zinc Drops Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 85
    The global Zinc Drops market was valued at US$ million in 2023 and is anticipated to reach US$ million by 2030, witnessing a CAGR of % during The forecast period 2024-2030. North American market for Zinc Drops is estimated to increase from $ million in 2023 to reach $ million by 2030, at a CAGR of % during The forecast period of 2024 through 2030. Asia-Pacific market for Zinc Drops is estimated to increase from $ million in 2023 to reach $ million by 2030, at a CAGR of % duri......
  • Global Anti-Infectives Market Research Report 2024
    Published: 10-Jan-2024        Price: US 2900 Onwards        Pages: 78
    The global Anti-Infectives market was valued at US$ 22700 million in 2023 and is anticipated to reach US$ 27480 million by 2030, witnessing a CAGR of 2.3% during The forecast period 2024-2030. The global pharmaceutical market is 1475 billion USD in 2022, growing at a CAGR of 5% during The next six years. The pharmaceutical market includes chemical drugs and biological drugs. For biologics is expected to 381 billion USD in 2022. In comparison, The chemical drug market is estima......
  • SERVICES
    Value for Money
    We believe in "optimum utilization of available budget and resources". While servicing our clients' (your) market research requirements, we keep the same approach in focus to help you get the best value for your $$s.
    Ever Growing Inventory
    Ranging from the smallest feasible / required data (datasheets, data facts, SWOT analysis, company profiles, etc) to full research reports that help you make decisions, our inventory is updated almost on a daily basis with the latest industry reports from domain experts that track more than 5000 niche sectors.
    One Stop Solution
    Need a custom research report on medical devices market? Require all available business intelligence on 3D printing industry? Exploring F&B sector of a particular country/region? RnRMarketResearch.com is your one-stop-solution to all market intelligence needs. We not only offer custom research and consulting services, we also "bundle" reports to meet your needs and help you fetch the data analysis you require for your business.
    Dedicated Client Engagement
    Not limited to only "finding" relevant reports for you, our client engagement team dedicates its efforts to understand your "business need" and accordingly maps available research data to help you move forward. Call "your" client engagement executive any time of your day and get your questions answered in order to make the correct business decision.
    Saving Time and Efforts
    Simply share your research requirement details with us and let us do all the hard work to find required intelligence for you. When you add up our "one stop solution" and "dedicated client engagement" services mentioned above, you obviously know the time and effort saving you do by working with us.
    Payment Flexibility
    Working with Fortune 500 organizations, we understand the importance of being flexible for payments. Share your payment terms with us and we will surely match up to them to ensure you get access to required business intelligence data without having to wait for the payment to be done.
    Post-Purchase Research Support
    Have questions after reading a report / datasheet bought through us? Not sure about the methodology used for data available in the research? Talk to us / Share your questions with us and if required, we will connect you with the analyst(s)/author(s) of the report(s) and ensure you get satisfactory answers for the same. Need more data / analysis / report(s) on the topic of your research/project? The RnRMarketResearch.com team is here for you 24X7 to support you with your post-purchase requirements. Subscription Offers & Packages (Get in touch with us for more details - [email protected] / +1 888 391 5441 )
    • Ad Hoc
    • Pay - as - you - go / Bucket Subscriptions
    • Fixed Cost for #of reports
    • Customize / Personalize as per your needs